Prognostic Value of KMT2A and Downstream Gene Expression in AML Patients Undergoing Allogeneic Hematopoietic Stem Cell Transplantation

AuthorSara Zehtabchehen
AuthorSahar Parkhidehen
AuthorMahshid Mehdizadehen
AuthorMohammad Hossein Mohammadien
AuthorDavood Bashashen
OrcidSara Zehtabcheh [0009-0006-5998-1722]en
OrcidSahar Parkhideh [0000-0001-7846-3222]en
OrcidMahshid Mehdizadeh [0000-0002-8937-5495]en
OrcidMohammad Hossein Mohammadi [0000-0002-8697-1371]en
OrcidDavood Bashash [0000-0002-8029-4920]en
Issued Date2025-12-31en
AbstractBackground: Relapse following allogeneic hematopoietic stem cell transplantation (allo-HSCT) remains a major cause of treatment failure in acute myeloid leukemia (AML). KMT2A, an epigenetic regulator, maintains hematopoietic homeostasis by modulating HOXA9, MEIS1, and PRDM16 — genes critical for leukemic stem cell (LSC) self-renewal. Objectives: The present study evaluated the expression of KMT2A and its downstream targets in AML patients post-allo-HSCT to assess their prognostic potential. Methods: Bone marrow (BM) samples from 42 participants (15 controls, 12 newly diagnosed AML, 15 post-HSCT AML) underwent RNA extraction, complementary DNA (cDNA) synthesis, and quantitative real-time PCR (qRT-PCR). Results: Significantly elevated expression of KMT2A and HOXA9 was observed in AML and HSCT-AML groups compared to controls (P < 0.0001). PRDM16 expression increased markedly only in de novo AML (P < 0.0001 vs. controls/HSCT-AML). MEIS1 showed no statistically significant differences across the groups; however, a non-significant increasing trend was observed in the de novo AML cohort. PRDM16 demonstrated exceptional diagnostic accuracy for AML (AUC = 0.966; sensitivity = 100%; specificity = 93.3%). Strong positive correlations existed between: KMT2A-PRDM16 (r = 0.818, P < 0.0001); KMT2A-HOXA9 (r = 0.680, P < 0.0001); HOXA9-PRDM16 (r = 0.699, P < 0.0001). Higher post-HSCT PRDM16 expression correlated with increased platelet counts (P = 0.019) and CD34+ cell doses (P = 0.032). Conclusions: PRDM16 is a highly sensitive and specific diagnostic biomarker for de novo AML. While KMT2A, HOXA9, and PRDM16 exhibit dysregulation in AML pathogenesis and post-HSCT, assessment of their expression at day +30 post-transplant did not predict early relapse. Integrating these genes into multi-parameter models or serial monitoring strategies may enhance prognostic utility.en
DOIhttps://doi.org/10.5812/ijcm-165616en
KeywordAcute Myeloid Leukemiaen
KeywordKMT2Aen
KeywordHOXA9en
KeywordMEIS1en
KeywordPRDM16en
KeywordPrognosisen
KeywordRelapseen
PublisherBrieflandsen
TitlePrognostic Value of KMT2A and Downstream Gene Expression in AML Patients Undergoing Allogeneic Hematopoietic Stem Cell Transplantationen
TypeResearch Articleen

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